Understanding Fabry Disease Therapy Choices Through the Eyes of the Patients
Sponsored by Amicus Therapeutics
About this trial
Last updated 2 years ago
Study ID
Status
Type
Placebo
Accepting
Not accepting
Trial Timing
Ended 2 years ago
What is this trial about?
What are the participation requirements?
Inclusion Criteria
- Participant must be a person with Fabry disease who is 18 years or older or the parent/legal guardian of a living person with Fabry disease who is under the age of 18 years or who are 18 years and older who are unable to answer for themselves.
- Confirmed diagnosis of Fabry disease with written proof of disease provided
- Must have a genetic mutation that is amenable to oral therapy
- Resident of Germany, the U.K or the U.S.
- Able to read, write and communicate in German, or English.
- Able to grant informed consent
- Willing to participate in a 50 to 60-minute telephone interview, including follow up questions (if necessary) and information regarding adverse events (if necessary).
Exclusion Criteria
- Inability to meet any of the inclusion criteria