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Evaluation of Maralixibat in Biliary Atresia Response Post-Kasai

Sponsored by Mirum Pharmaceuticals, Inc.

About this trial

Last updated 2 years ago

Study ID

MRX-701

Status

Active, not recruiting

Type

Interventional

Phase

Phase 2

Placebo

Yes

Accepting

18-75 Years
21 to 111 Years
All
All

Not accepting

Not accepting
Healthy Volunteers

Trial Timing

Ended 5 months ago

What is this trial about?

A study to evaluate the efficacy and safety of maralixibat in infants with Biliary Atresia (BA) after Hepatoportoenterostomy (HPE, also known as the Kasai procedure).

What are the participation requirements?

Yes

Inclusion Criteria

1. Male or female subjects with body weight ≥2500 g, who are ≥21 days old and <90 days old at the time of HPE (Kasai)

2. HPE or Kasai Procedure within 3 weeks prior to randomization

3. Clinical diagnosis of biliary atresia

No

Exclusion Criteria

1. Subjects with intractable chronic diarrhea at randomization

2. Subjects not tolerating enteral feeds at randomization

3. History of ileal resection

4. Diagnosis of biliary atresia splenic malformation syndrome or cystic biliary atresia

5. Evidence of another non-biliary atresia pathology involving the intrahepatic bile duct (e.g., paucity, sclerosing cholangitis)

6. Evidence of liver failure (e.g. significant ascites)

Locations

Location

Status